NORD Rare Diseases and Orphan Products Breakthrough Summit

The NORD Rare Diseases and Orphan Products Breakthrough Summit is a pivotal event that aims to shape the future of treatments, research, and policy for rare diseases. Taking place in Washington, DC, this summit brings together a diverse group of stakeholders including researchers, pharmaceutical companies, medical professionals, and families affected by rare disorders. With over 30 million Americans and more than 400 million people worldwide living with rare diseases, the summit serves as a platform for fostering critical discussions and forging valuable partnerships aimed at advancing innovation and equitable access to rare disease research.Attendees can expect to engage with influential voices in the rare disease community, learn about groundbreaking advancements that improve access to clinical trials, and discover emerging trends that are likely to reshape the rare disease landscape. The summit has previously featured esteemed speakers such as U.S. Senator Amy Klobuchar of Minnesota and representatives from leading organizations like the American Society for Gene & Cell Therapy (ASGCT) and Children’s Hospital at Montefiore Einstein. Participants have expressed the summit's significant impact, highlighting the electric atmosphere filled with purpose and unity, and the immense value of the insights gained through presentations and conversations with experts. NORD emphasizes the independence and integrity of their educational content, ensuring that discussions remain free from external influences, thereby focusing solely on the advancement of care, research, and advocacy for those impacted by rare diseases.