NORD Rare Diseases and Orphan Products Breakthrough Summit

The NORD Rare Diseases and Orphan Products Breakthrough Summit serves as a pivotal platform for fostering critical discussions and forging valuable partnerships aimed at advancing equitable access to rare disease research. By connecting influential voices and stakeholders who are shaping the future of rare disease treatments, research, and policy, the summit focuses on learning about cutting-edge advancements that improve access to clinical trials and discovering emerging trends that could redefine the landscape of rare diseases. The event draws notable leaders and innovators from the field, including representatives from the American Society for Gene & Cell Therapy (ASGCT) and U.S. Senator Amy Klobuchar of Minnesota, alongside key institutions like Children’s Hospital at Montefiore Einstein.Past attendees have echoed the significance of this gathering, describing it as a 'world-class event' that unites researchers, pharmaceutical companies, medical professionals, and families affected by rare disorders. With nearly 1,000 participants, each contributing unique stories and perspectives, the atmosphere is charged with purpose and unity. Attendees have highlighted the invaluable experience gained, particularly students who have noted the inspiring presentations and insightful conversations with experts in the rare disease community. The summit provides an incredible platform for sharing stories, addressing the unmet needs of the rare disease community, and advancing the dialogue around better care, research, and advocacy. NORD emphasizes the integrity and independence of its educational content, ensuring that sessions are developed without influence from industry partners or external commercial interests, driven solely by the expertise of NORD staff and planning committees. This commitment aligns with NORD's mission to improve the health and well-being of people with rare diseases through advances in care, research, and policy.